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Emily N
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Join date: Dec 27, 2023
Posts (3)
Apr 9, 2025 ∙ 1 min
Toddler Treated for OTC with an Innovative Gene Therapy
By Andrew Xia A 14-month-old boy, Tomas, has recently become the first patient ever to receive a groundbreaking gene therapy treatment...
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Oct 4, 2024 ∙ 2 min
FDA’s Recent Grants Boost Rare Disease Research and Treatments
Written by Harper Winslow The FDA has made significant strides in advancing rare disease research by recently awarding $17.2 million...
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Feb 9, 2024 ∙ 1 min
Rare Disease Day 2024
Written by Sandrea Delgado Rare disease day is celebrated annually on the last day of February to serve as a reminder of the challenges...
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